2024-07-22
»ùÒòÖÎÁÆÓÐÊýÐ¡»ñÏ£Íû£¬£¬£¬»ò¸Ä±äÎÞÒ©¿ÉÓÃÊ±ÊÆ£¿£¿£¿£¿£¿
ÍâµØÊ±¼ä2024Äê7ÔÂ15ÈÕ£¬£¬£¬ÃÀ¹úLexeo Therapeutics¹«Ë¾Ðû²¼Æä¸¥ÀïµÂÀµÏ£¹²¼Ãʧµ÷£¨Friedreich Ataxia£¬£¬£¬FA£©Ð¡»ùÒòÁÆ·¨LX2006µÄ×îÐÂÏ£Íû£ºÔÚÒ»Ïî1/2ÆÚÁÙ´²ÊÔÑéºÍÒ»ÏîÃÀ¹úÍþ¶û¿µÄζûҽѧԺ£¨Weill Cornell Medicine£©Ñо¿ÕßÌᳫµÄ 1aÆÚÁÙ´²ÊÔÑéÖУ¬£¬£¬LX2006ÄÍÊÜÐÔÓÅÒ죬£¬£¬Ã»ÓÐÓëÖÎÁÆÏà¹ØµÄÑÏÖØ²»Á¼ÊÂÎñ£¬£¬£¬ÐÄÔàÉúÎï±ê¼ÇÎï·ºÆð¾ßÓÐÁÙ´²ÒâÒåµÄ¸ÄÉÆ£¬£¬£¬²¢ÇÒÕâЩ¸ÄÉÆËæ×Åʱ¼äµÄÍÆÒÆ¶øÔöÌí¡£¡£¡£¡£
ÔĶÁ¸ü¶à